Plasma
Exchange Versus Intravenous Immunoglobulin in Children
with Guillain Barre
Syndrome
ABSTRACT
Objective:
To compare
the outcome of plasma exchange versus intravenous immunoglobulin among children
with Guillain Barre
Syndrome.
Methods: A comparative
experimental study was conducted at department of Pediatrics, National
Institute of Child Health, Karachi from August 2016 to February 2017. All
patients of age ranged from 2-15 years of either gender having duration of Guillain Barre Syndrome not more
than 14 days were included. The children were divided into plasma exchange or intravenous
immunoglobulin group. Intravenous immunoglobulin was administered for
five days in a dose of 0.4 g/kg/day/ while a daily one-volume plasma exchange
was given to patients in the plasma exchange group for five days. Duration of
mechanical ventilation and the pediatric intensive care unit stay in days were
noted.
Results: Of 78
children, the mean age was 6.64 +-3.06 years.
There were 47 (60.3%) males and 31 (39.7%) females. A significantly higher
length of intensive care unit stay was noted among children who received plasma
exchange (9.45 +-4.59 days) as compared to the children who
received intravenous immune globin (4.97 +-2.84 days)
(p-value <0.001, 95% CI -6.23 to -2.73). Similarly, the mean duration of
ventilator stay was significantly higher among children who received plasma
exchange (7.33 +-3.44 days) as compared to the children who
received intravenous immune globin (2.01 +-0.01 days)
(p-value <0.001, -7.91 to -2.74).
Conclusion: The outcome of intravenous immune globin founds better than
that of plasma exchange in treating children with Guillain
Barre syndrome.
Keywords: Plasma exchange, Intravenous immunoglobulin, Children, Guillain Barre syndrome.
INTRODUCTION
The
occurrence of Guillain-Barre syndrome is frequently observed due to
neuromuscular paralysis at all ages with 1.2-2.3 per 100,000 occurrences per
year.1 Globally, the disease is emerged as
a post-infectious disorder, which is mostly recognized as Campylobacter jejuni infection.2 In addition, Haemophilus influenza, Epstein-Barr virus, Mycoplasma
pneumonia, and cytomegalovirus are also other infections associated with Guillain Barre Syndrome. It has
been found that the incidence of Guillain Barre Syndrome is reported after operations, stressful
events or vaccinations, but the pathophysiology and causality are still scarce.3
However,
it is still not commonly found among children and possess a milder course.4,5 This is unspecific and there are no identified
differences in its pathology or electrophysiology from Guillain
Barre Syndrome among adults so that there are no
anticipated differences in treatment response.6,7 In addition,
including intravenous immunoglobulin did not make a substantial difference to
any outcome after plasma exchange in the largest trial. Corticosteroids are
ineffective in spite of the effectiveness of intravenous immunoglobulin as well
as plasma exchange even though other coincident medical conditions are not
effective. 8,9
The rationale of the study is there is dearth of randomized
controlled trial locally as well as internationally and secondly having
conflicting results.10 Therefore the present study is designed to
assess the outcome between Plasma exchange and intravenous immunoglobulin. The
better of the two modalities is used in future considering the resource-poor
settings and limited facilities available in our country.
METHODS
This
comparative experimental study was conducted at department of Pediatrics,
National Institute of Child Health, Karachi from August 2016 to February 2017. The study was conducted after obtaining approval from the research
evaluation unit of College of Physician and Surgeon of Pakistan. Signed
informed consent was also obtained from the parents/guardians after explaining the purpose, procedure, risk and benefits of the study
and confidentiality was ensured.
The
presence of progressive weakness in both arms and legs assessed on MRC sum
scores and score less than 5 was taken as progressive weakness along with are flexia (or decreased tendon reflexes) was labeled as Guillain Barre
syndrome positive.
All patients
of age ranging from 2-15 years of either gender having Guillain
Barre Syndrome with muscle weakness and had duration
of Guillain Barre Syndrome
not more than 14 days were consecutively enrolled. Children with history of
myasthenia for >14 days prior to mechanical ventilation, intravenous
immunoglobulin or plasma exchange started prior to inclusion in the study, injury to >6 muscle groups and non-consenting
parents were excluded.
The sample
size calculated using WHO sample size calculator using significance level =5%,
power= 80%, reported mean pediatric intensive care unit stay in patients with
intravenous immunoglobulin: 16.5 +- 2.1, reported mean intensive care unit
length of stay in patients with plasma exchange: 15.0 +- 2.6 (6). The final
sample size came out to be 78 patients, i.e. 39 in each group.
Brief history
regarding the duration of disease along with demographics details was taken from
the parents. The children were divided into two groups by asking the parents to
pick one sealed opaque envelop bearing a card of plasma exchange or intravenous
immunoglobulin, at the time of inclusion. Endotracheal mechanical ventilation
was used to ventilate all patients. If children were not able to protect their
airway, they had increased work of breathing, showed CO2 retention, had PaO2 as
compared to 70 mmHg in room air requiring extra FiO2 they were intubated. A T
piece was used for 2 hours to perform a daily spontaneous breathing trial, if
intact was reflexed by airway and secretions were managed. If SBT was
successful, patients were extubated. If there was increased working of
breathing, SpO2, pH, and PaCO2 remained close to pre-SBT value, and tachycardia,
the SBT was observed to be successful. The attending consultant having based on
his 5 years of experience make an independent decision regarding the
initiation, weaning, and terminating mechanical ventilation.
Intravenous
immunoglobulin was administered for five days in a dose of 0.4 g/kg/day.
One-volume plasma exchange for 5 consecutive days was offered to patients in
the plasma exchange group on a regular basis. The duration of mechanical
ventilation and the pediatric intensive care unit in days were included in the
primary outcome. This information was observed with the demographics, which
include weight, duration of symptoms, gender, height, and age.
SPSS version
21 was used to enter and analyze the data. Quantitative variables like age,
weight, height, length of stay in intensive care unit, and duration of
mechanical ventilation were calculated through Mean +- standard deviation. The two groups plasma exchange and
intravenous immunoglobulin were compared in terms of pediatric intensive
care unit stay in days and duration of mechanical ventilation by applying unpaired t test. p-value
less than or equal to 0.05 was taken as significant.
All procedures followed were in accordance
with the ethical standards of the responsible committee on human experimentation
(institutional and national) and with the Helsinki Declaration of 1975, as
revised in 2008.
RESULTS
Majority of
the patients 47 (60.3%) were presented with ≤7 years of age (Mean age
6.64 +-3.06 years) years. There were 47 (60.3%) males and 31 (39.7%) females.
Mean height, weight and BMI of the patients were 111.82 +-19.92 cm, 21.05
+-7.32 kg and 16.28 +-1.52 kg/m2. Most of the patients 50 (64.1%)
had ≤18.5 kg/m2 BMI. Mean duration of symptoms was 2.18 +-2.20 days.
Majority of the patients 74 (94.9%) were presented with ≤5 days of
duration of symptoms.
Significant
difference of age (p-value <0.001), height (p-value <0.001), weight and
duration of symptoms (p-value 0.006) was observed in between both groups.
(Table 1)
Mean
duration of stay in pediatric intensive care unit was 7.09 +-4.37 days. The mean duration of pediatric intensive care
unit stay was significantly higher among children who received plasma exchange
(9.45 +-4.59 days) as compared to
the children who received intravenous immune globin (4.97 +-2.84 days) (p-value
<0.001, 95% CI -6.23 to -2.73). Similarly, the mean duration of ventilator
stay was significantly higher among children who received plasma exchange (7.33 +-3.44 days) as compared to the
children who received intravenous immune globin (2.01 +-0.01 days) (p-value
<0.001, -7.91 to -2.74). (Table 2, 3)
DISCUSSION
It has
stated in literature that plasma exchange and intravenous immunoglobulin are
effective immunotherapies for patients with Guillain Barre Syndrome, if both immunotherapies are provided within
the first few weeks of disease.11 Plasma exchange is mostly
administered as one plasma volume for Guillain Barre Syndrome patients over 1 to 2 weeks on 5 separate
occasions.11 This study was conducted to assess the individual role
of both therapies in terms of length of intensive care unit and mechanical
ventilation stay.
The
finding of this study showed that the mean
duration of pediatric intensive care unit stay was significantly higher among
children who received plasma exchange as compared to the children who received
intravenous immune globin. Similarly, the mean duration of ventilator stay was
significantly higher among children who received plasma exchange as compared to
the children who received intravenous immune globin. Somewhat similar finding
was reported in a study conducted by Gajjar et al.13 The author stated that in children with Guillain bar Syndrome, plasma exchange was demonstrated to
be efficient as first line or adjunctive therapy. It is secure if quantity
changes, supplementation of calcium and access to veins are taken care of.13
However, Hughes et al in their systematic review has reported no obvious
difference between plasma exchange and intravenous immunoglobulin.14
Several studies suggested that children affected by Guillain Barre Syndrome should
receive a normal intravenous immunoglobulin course, as well as a normal plasma
exchange course of five successive days.15-17 A study by Ye et al
conducted in China has reported that after plasma exchange treatment, nerve
function defect appeared to improve better than as compared to patients who
received intravenous immunoglobulin group. Moreover, the clinical effect was
also better than the immunoglobulin group. The author also stated that both
plasma and intravenous immunoglobulin exchange have an elevated therapeutic
reaction and are sensible therapeutic choices for Guillain
Barre Syndrome.17 Gajjar et al has reported inadequate vascular
access as the common complication of plasma exchange.13 However, in a study conducted by Rekha et al, the most common
complication was allergic reactions to fresh frozen plasma.18 In spite of this, plasma exchange is
reported to be more curative as it can enhance the symptoms efficiently and
help patients in their early rehabilitation.13,19,20
A study investigated complications among adults with
neurological disorders who received plasma exchange. According the study
findings, hypotension, allergic reactions, and vomiting were some the findings
and the frequency ranged from 11-2%.21 In another study, complication
during plasma exchange procedure reported as 18.3%. These complications were
catheter placement procedure, hypotension, hypocalcaemia, and allergic
reactions.22 However, in the current study,
we failed to collect the information regarding complications.
This study has certain limitations,
firstly the sample size of the study was small. Secondly, the study has not
reported certain important variables like complications, outcomes. Future
research should conduct randomized controlled trials well as appropriately
designed cohort studies for comparing the outcome after several treatment
regimens undertaking significant numbers of patients. Despite of the mentioned
limitations, this study has given local insight of plasma exchange in children
with GBS. A though literature search has reported, previously most of the
studies were conducted on adult patient with GBS. In these studies, no
significant difference in the outcome was noted among GBS patients receiving
plasma exchange versus the intravenous immunoglobulin. 23,24
CONCLUSION
The outcome of intravenous immune globin founds better than
that of plasma exchange in treating children with Guillain
Barre syndrome.
Table 1: Clinical characteristics of the
patients (n=78) |
||
IVIG |
PE |
|
Clinical characteristics |
mean +-SD |
mean +-SD |
Age, years |
4.10 +-1.69 |
9.17 +-1.20 |
Height, cm |
95.33 +-13.78 |
128.31 +-7.49 |
Weight, kg |
15.30 +-4.02 |
26.79 +-4.95 |
Duration of symptoms, days |
1.51 +-0.51 |
2.86 +-2.93 |
IVIG: Intravenous immunoglobulin, PE: Plasma Exchange All data presented as mean +- SD. Independent t-test applied,
p-value <0.05 taken as significant |
Table 2: Mean difference of duration of PICU
stay in both group (n=78) |
|||
Group |
Duration of PICU stay (in days) |
||
Mean +-SD |
p-value |
95% CI |
|
IVIG |
<0.001 |
||
PE |
|||
IVIG: Intravenous immunoglobulin,
PE: Plasma Exchange All data presented as
mean +- SD. Independent t-test applied, p-value <0.005 taken as
significant |
Table 3: Mean difference of duration of
ventilator stay in both group (n=78) |
|||
Group |
Duration of ventilator stay (in days) |
||
Mean +-SD |
p-value |
95% CI |
|
IVIG |
<0.001 |
||
PE |
|||
IVIG: Intravenous
immunoglobulin, PE: Plasma Exchange All data presented as mean
+- SD. Independent t-test applied, p-value <0.005 taken as significant |
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